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A glycolipid metabolic disorder treating agent

2025-06-19 07:214190下载
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PROBLEM TO BE SOLVED : To provide a glycolipid metabolic abnormality treating agent useful to glycolipid metabolic abnormality caused by human β-galactosidase gene mutations.SOLUTION : The invention provides a treating agent of glycolipid metabolic abnormality caused by β-galactosidase gene mutations which contains as an active ingredient a conduramine F-4 derivative represented by the formula (1) or a pharmaceutically acceptable salt thereof. (Rand Rare each independently H or an alkyl group, an alkenyl group, an alkynyl group, and an acyl group and the like; Rto Rare each independently a hydroxyl group having a substituent selected from a hydroxyl group or an alkyl group, an acyl group, a silyl group, an aralkyl group, an alkoxyalkyl group, and an aralkyloxy alkyl group.)


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